Therapeutic Potential of CFTR Correctors (C17) for Rare Muscle Disorders
Publicado por:Unknown
·Publicado em: 2025-12-13
Discussion regarding how CFTR correctors, such as C17, can be utilized to treat rare inherited muscle disorders like Brody myopathy and limb-girdle muscular dystrophy type 2E/R4.
Carregando...